SNP-based Microdeletion and Aneuploidy RegisTry (SMART) Read more about SNP-based Microdeletion and Aneuploidy RegisTry (SMART)
VTS-270 to Treat Niemann-Pick Type C1 (NPC1) Disease Read more about VTS-270 to Treat Niemann-Pick Type C1 (NPC1) Disease
Once-Nightly Sodium Oxybate for Treatment of Excessive Daytime Sleepiness and Cataplexy in Narcolepsy Read more about Once-Nightly Sodium Oxybate for Treatment of Excessive Daytime Sleepiness and Cataplexy in Narcolepsy
An Open Label Study of CM-AT for the Treatment of Children With Autism Read more about An Open Label Study of CM-AT for the Treatment of Children With Autism
A Study to Look at Tapentadol Oral Solution in Children and Adolescents in Pain Read more about A Study to Look at Tapentadol Oral Solution in Children and Adolescents in Pain
ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) Read more about ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)
A Randomized Study of Three Medication Regimens for Acute Low Back Pain Read more about A Randomized Study of Three Medication Regimens for Acute Low Back Pain
Childhood Absence Epilepsy Rx PK-PD-Pharmacogenetics Study Read more about Childhood Absence Epilepsy Rx PK-PD-Pharmacogenetics Study
Naltrexone for Use in Conjunction With Buprenorphine in Adults With Opioid Use Disorder Prior to First Dose of VIVITROL® (Naltrexone for Extended-Release Injectable Suspension) Read more about Naltrexone for Use in Conjunction With Buprenorphine in Adults With Opioid Use Disorder Prior to First Dose of VIVITROL® (Naltrexone for Extended-Release Injectable Suspension)