Efficacy and Safety of Odevixibat in Children With Biliary Atresia Who Have Undergone a Kasai HPE (BOLD) Read more about Efficacy and Safety of Odevixibat in Children With Biliary Atresia Who Have Undergone a Kasai HPE (BOLD)
An Open Label Study of FT218 in Subjects With Narcolepsy Read more about An Open Label Study of FT218 in Subjects With Narcolepsy
Study of Sparsentan in Patients With Primary Focal Segmental Glomerulosclerosis (FSGS) Read more about Study of Sparsentan in Patients With Primary Focal Segmental Glomerulosclerosis (FSGS)
Study Assessing CLENPIQ as Bowel Preparation for Pediatric Colonoscopy Read more about Study Assessing CLENPIQ as Bowel Preparation for Pediatric Colonoscopy
Long-term Safety of Linaclotide in Pediatric Participants With FC or IBS-C Read more about Long-term Safety of Linaclotide in Pediatric Participants With FC or IBS-C
Post-trial Access for Nipocalimab in Participants With Warm Autoimmune Hemolytic Anemia (wAIHA) Read more about Post-trial Access for Nipocalimab in Participants With Warm Autoimmune Hemolytic Anemia (wAIHA)
A Safety and Efficacy Study of a Range of Linaclotide Doses Administered Orally to Children Ages 7-17 Years, With Irritable Bowel Syndrome With Constipation Read more about A Safety and Efficacy Study of a Range of Linaclotide Doses Administered Orally to Children Ages 7-17 Years, With Irritable Bowel Syndrome With Constipation
ACURATE IDE: Safety and Effectiveness Study of ACURATE Valve for Transcatheter Aortic Valve Replacement Read more about ACURATE IDE: Safety and Effectiveness Study of ACURATE Valve for Transcatheter Aortic Valve Replacement
MEK Inhibitor Mirdametinib (PD-0325901) in Patients With Neurofibromatosis Type 1 Associated Plexiform Neurofibromas Read more about MEK Inhibitor Mirdametinib (PD-0325901) in Patients With Neurofibromatosis Type 1 Associated Plexiform Neurofibromas
Reduced Intensity Haploidentical BMT for High Risk Solid Tumors Read more about Reduced Intensity Haploidentical BMT for High Risk Solid Tumors