A Phase 2 Basket Study of Vosoritide in Children With Turner Syndrome, SHOX Deficiency and Noonan Syndrome With an Inadequate Response to Human Growth Hormone Read more about A Phase 2 Basket Study of Vosoritide in Children With Turner Syndrome, SHOX Deficiency and Noonan Syndrome With an Inadequate Response to Human Growth Hormone
Bone in CKD Alkali Response (BICARb Pilot Trial) Read more about Bone in CKD Alkali Response (BICARb Pilot Trial)
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program Read more about ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
Study Of Palbociclib Combined With Chemotherapy In Pediatric Patients With Recurrent/Refractory Solid Tumors Read more about Study Of Palbociclib Combined With Chemotherapy In Pediatric Patients With Recurrent/Refractory Solid Tumors
A Randomized Trial of NSAID Dosing Strategies Read more about A Randomized Trial of NSAID Dosing Strategies
Telehealth CBT for Adolescents and Young Adults With Childhood-onset Systemic Lupus Erythematosus Read more about Telehealth CBT for Adolescents and Young Adults With Childhood-onset Systemic Lupus Erythematosus
A Study of Ustekinumab or Guselkumab in Pediatric Participants With Active Juvenile Psoriatic Arthritis Read more about A Study of Ustekinumab or Guselkumab in Pediatric Participants With Active Juvenile Psoriatic Arthritis
Comparing Inpatient COVID-19 Outcomes in 2 Different PT Dosing Groups Read more about Comparing Inpatient COVID-19 Outcomes in 2 Different PT Dosing Groups
The PRIORi-T Trial--Prospective Randomized Investigation of Radiofrequency Targeted Vertebral Augmentation Read more about The PRIORi-T Trial--Prospective Randomized Investigation of Radiofrequency Targeted Vertebral Augmentation
IGFD Registry: A Patient Registry for Monitoring Long-term Safety and Efficacy of Increlex Read more about IGFD Registry: A Patient Registry for Monitoring Long-term Safety and Efficacy of Increlex