Low Dose Oral Methotrexate in Pediatric Crohn's Disease Patients Initiating Anti-Tumor Necrosis Factor (Anti-TNF) Therapy Read more about Low Dose Oral Methotrexate in Pediatric Crohn's Disease Patients Initiating Anti-Tumor Necrosis Factor (Anti-TNF) Therapy
Effectiveness and Safety of Dysport® (abobotulinumtoxinA) in Paediatric Lower Limb Spasticity Read more about Effectiveness and Safety of Dysport® (abobotulinumtoxinA) in Paediatric Lower Limb Spasticity
Study to Evaluate the Effect of Voxelotor Administered Orally to Patients With Sickle Cell Disease (GBT_HOPE) Read more about Study to Evaluate the Effect of Voxelotor Administered Orally to Patients With Sickle Cell Disease (GBT_HOPE)
Gene Transfer Clinical Study in Crigler-Najjar Syndrome Read more about Gene Transfer Clinical Study in Crigler-Najjar Syndrome
Safety and Efficacy of Apixaban in Severe Renal Impairment Read more about Safety and Efficacy of Apixaban in Severe Renal Impairment
An Open Label Evaluation of the Safety and Pharmacokinetics of Ganciclovir in Children Read more about An Open Label Evaluation of the Safety and Pharmacokinetics of Ganciclovir in Children
Observational Study of Obstructive Lung Disease (NOVELTY) Read more about Observational Study of Obstructive Lung Disease (NOVELTY)
A Long-term Active Treatment Study of Mongersen (GED-0301) in Subjects With Crohn's Disease Read more about A Long-term Active Treatment Study of Mongersen (GED-0301) in Subjects With Crohn's Disease
Triheptanoin (C7 Oil), a Food Supplement, for Glucose Transporter Type I Deficiency (G1D) Read more about Triheptanoin (C7 Oil), a Food Supplement, for Glucose Transporter Type I Deficiency (G1D)
Clinical Assessment Study in Crigler-Najjar Syndrome Read more about Clinical Assessment Study in Crigler-Najjar Syndrome